The episodic ataxia treatment market has seen considerable growth due to a variety of factors.
• The episodic ataxia treatment market has seen strong growth in recent years. It will grow from $11.07 billion in 2024 to $11.83 billion in 2025, at a CAGR of 6.9%.
The growth is attributed to a better understanding of genetic causes, increased funding for rare disease research, more specialized clinics, greater awareness of personalized medicine, and higher participation in clinical trials.
The episodic ataxia treatment market is expected to maintain its strong growth trajectory in upcoming years.
• The episodic ataxia treatment market is projected to grow steadily, reaching $15.21 billion by 2029 at a CAGR of 6.5%.
The growth is attributed to increased accessibility to genetic testing, rising demand for genetic counseling, growing clinical trials, expanding patient registries, and more investments in rare disease biobanks. Trends include technological advancements, personalized medicine, telemedicine, stem cell therapy, and telerehabilitation services.
The growing occurrence of neurological disorders is likely to drive the growth of the episodic ataxia treatment market in the future. Neurological disorders impact the central and peripheral nervous systems, including the brain, spinal cord, nerves, and muscles. Contributing factors include an aging population, genetic influences, and infections. Episodic ataxia treatment aims to manage symptoms related to the loss of coordination and balance. For example, in April 2022, the European Brain Council reported that dementia affected 10.5 million people in Europe in 2022, with a forecast to rise to 18.7 million by 2050. This increasing prevalence supports market growth.
The episodic ataxia treatment market covered in this report is segmented –
1) By Type: Ataxia telangiectasia, Episodic ataxia, Spinocerebellar ataxia, Friedreich’s ataxia, Other Types
2) By Treatment: Medications, Levodopa, Pramipexole, Venlafaxine, Other Treatments
3) By Route of Administration: Oral, Parenteral, Other Routes of Administration
4) By Distribution Channel: Direct Tender, Retail Sales, Other Distribution Channels
5) By End User: Hospital, Clinics, Home Healthcare, Other End Users
Subsegments
1) By Ataxia Telangiectasia: Neurological Complications, Immunodeficiency, Cancer Susceptibility
2) By Episodic Ataxia: Type 1 (EA1), Type 2 (EA2), Other Subtypes
3) By Spinocerebellar Ataxia: Type 1 (SCA1), Type 2 (SCA2), Type 3 (SCA3), Type 6 (SCA6), Type 7 (SCA7), Type 17 (SCA17), Other Types
4) By Friedreich’s Ataxia: Early-onset Friedreich’s Ataxia, Late-onset Friedreich’s Ataxia, Other Types
5) By Other Treatments: Supportive Care (Physical Therapy, Occupational Therapy), Symptomatic Treatment (Muscle Relaxants, Dopaminergic Medications)
Major companies in the episodic ataxia treatment market are focused on developing innovative treatments, such as Friedreich's ataxia (FA) therapies, to improve patient outcomes and address unmet needs related to this rare neurological disorder. Episodic ataxia (EA) is characterized by intermittent ataxia episodes and lack of voluntary coordination of muscle movements, with varying frequency and severity. For example, in February 2024, Biogen Inc. announced the approval of SKYCLARYS (omaveloxolone) for treating FA. Omaveloxolone addresses mitochondrial dysfunction in FA, potentially altering the disease’s progression, rather than just easing symptoms. It works as a potent transcriptional modulator to restore mitochondrial function and cellular energy production.
Major companies operating in the episodic ataxia treatment market are:
• Pfizer Inc.
• AbbVie Inc.
• Sanofi
• Bristol-Myers Squibb Company
• Novartis AG
• Takeda Pharmaceutical Company Limited
• Merck KGaA
• Banner Health
• Astellas Pharma Inc.
• Daiichi Sankyo Company Limited
• UCB S.A.
• Ipsen
• BioMarin Pharmaceutical Inc.
• Neurocrine Biosciences Inc.
• PTC Therapeutics Inc.
• Kissei Pharmaceutical Co. Ltd.
• Catalyst Pharmaceuticals Inc.
• Design Therapeutics Inc.
• Larimar Therapeutics Inc.
• Voyager Therapeutics Inc.
• Capsida Biotherapeutics Inc.
• Adverum Biotechnologies Inc.
• CRISPR Therapeutics AG
North America was the largest region in the episodic ataxia treatment market in 2023. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in the episodic ataxia treatment market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa.