The Leber Congenital Amaurosis Market Overview 2025 report reveals that the market size has grown significantly over the past few years, with projections indicating further expansion.
The Leber Congenital Amaurosis Global Market Report 2025 showed a significant growth trend. The market expanded from $1.01 billion in 2024 to reach $1.07 billion in 2025, reflecting a compound annual growth rate (CAGR) of 6.0%.
The Leber Congenital Amaurosis market is predicted to reach $1.34 billion by the year 2029, growing at a compound annual growth rate (CAGR) of 5.9%.
Download Your Free Sample of the 2025 Leber Congenital Amaurosis Market Report and Uncover Key Trends Now!The key drivers in the leber congenital amaurosis market are:
• Growing investment in gene therapy
• Increasing prevalence of inherited retinal diseases
• Regulatory approvals for novel treatments
• Expanding clinical trials and rising healthcare expenditure
The leber congenital amaurosis market covered in this report is segmented –
1) By Treatment Type: Gene Therapy, Pharmaceutical Drugs, Retinal Prosthesis, Assistive Devices, Other Treatments
2) By Age Of Onset: Congenital Leber Congenital Amaurosis (LCA) (From Birth), Early Childhood Leber Congenital Amaurosis (LCA) (1-5 Years), Late-Onset Leber Congenital Amaurosis (LCA) (6 Years And Above)
3) By Distribution Channel:, Direct Tender, Retail Sales
4) By End User: Hospitals, Specialized Eye Clinics, Ophthalmology Research Centers, Home Care Settings, Other End Users
Subsegments:
1) By Gene Therapy: RPE65 Gene Replacement Therapy, CRISPR-Based Gene Editing, AAV (Adeno-Associated Virus) Vector Therapy, Emerging Experimental Gene Therapies
2) By Pharmaceutical Drugs: Retinoid-Based Therapies, Neuroprotective Agents, Anti-Inflammatory Drugs, Antioxidant Therapies
3) By Retinal Prosthesis: Implantable Retinal Chips, Artificial Retinal Stimulation Devices, Bionic Eye Technology
4) By Assistive Devices: Low Vision Aids, Screen Readers and Braille Devices, Mobility Aids for Vision Impairment
5) By Other Treatments: Stem Cell Therapy, Optogenetics-Based Treatments, Visual Rehabilitation Programs, Nutritional and Dietary Interventions
The key trends in the leber congenital amaurosis market are:
• Emerging CRISPR-based treatments are shaping the future of the Leber Congenital Amaurosis market.
• Growing trends of collaboration between biotech firms are expected to impact the market.
• The development of personalized medicine is becoming a significant trend in this market.
• Technological advancements in retinal imaging and expansion of teleophthalmology are also significant emerging trends.
Major players in the leber congenital amaurosis market are:
• Sanofi S.A.
• Novartis AG
• Astellas Pharma Inc.
• Invitae Corporation
• Novelion Therapeutics Inc.
• Andelyn Biosciences Inc.
• CD Genomics Inc.
• Editas Medicine Inc.
• MeiraGTx Holdings plc
• Sangamo Therapeutics Inc.
• LKC Technologies Inc.
• Aldeyra Therapeutics Inc.
• Asper Biogene OÜ
• Allergan Inc.
• ProQR Therapeutics N.V.
• GenSight Biologics S.A.
• Ocugen Inc.
• IVERIC bio Inc. (formerly Ophthotech Corporation)
• Atsena Therapeutics Inc.
• HuidaGene Therapeutics Co. Ltd.
North America was the largest region in the leber congenital amaurosis market in 2024