Contact Us
Gene Therapy For Inherited Genetic Disorders Global Market Report 2025
Global Gene Therapy For Inherited Genetic Disorders Market Report 2025
Item added to cart!

Published : December 2025

Pages : 250

Format : PDF

Delivery Time : 2-3 Business Days

Report Price : $4490.00

Purchase This Report Download Sample PDF
Purchase This Report

Gene Therapy For Inherited Genetic Disorders Global Market Report 2025

By Type (Viral Vector-Based Therapies, Gene Editing Techniques, Ribonucleic Acid-Based Therapies, Ex Vivo Gene Therapy), By Application (Inherited Metabolic Disorders, Neurological Disorders, Cardiovascular Disorders, Musculoskeletal Disorders, Ophthalmic Disorders), By End-User (Hospitals, Specialty Clinics, Research Institutes, Other End-Users) - Market Size, Trends, And Global Forecast 2025-2034

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report’s Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

Gene Therapy For Inherited Genetic Disorders Market Overview

• Gene Therapy For Inherited Genetic Disorders market size has reached to $3.39 billion in 2024

• Expected to grow to $8.15 billion in 2029 at a compound annual growth rate (CAGR) of 19.1%

• Growth Driver: Rising Demand For Personalized Medicine Driving Growth In The Market Due To Advancements In Genetic Technologies

• Market Trend: Advancing Targeted Gene Therapies For Rare Inherited Genetic Disorders

North America was the largest region in 2024 and Asia-Pacific is the fastest growing region.

What Is Covered Under Gene Therapy For Inherited Genetic Disorders Market?

Gene Therapy for inherited genetic disorders is a medical strategy that targets the root cause of hereditary diseases by repairing or replacing faulty genes. Its main goal is to provide a potential cure rather than merely alleviating symptoms. It introduces functional genes into a patient’s cells, restores normal cell function, and improves overall health. This approach shows significant promise for treating rare genetic disorders, offering the possibility of long-lasting or permanent therapeutic effects.

The main types of gene therapy for inherited genetic disorders are viral vector-based therapies, gene editing techniques, ribonucleic acid-based therapies, and ex vivo gene therapy. Viral vector-based therapies use genetically modified, non-replicating viruses to deliver therapeutic genetic material into patient cells for treating diseases. These therapies are applied in various applications such as inherited metabolic disorders, neurological disorders, cardiovascular disorders, musculoskeletal disorders, and ophthalmic disorders and used by several end users, including hospitals, specialty clinics, research institutes, and others.

Gene Therapy For Inherited Genetic Disorders Market Size and growth rate 2025 to 2029: Graph

What Is The Gene Therapy For Inherited Genetic Disorders Market Size 2025 And Growth Rate?

The gene therapy for inherited genetic disorders market size has grown rapidly in recent years. It will grow from $3.39 billion in 2024 to $4.05 billion in 2025 at a compound annual growth rate (CAGR) of 19.4%. The growth in the historic period can be attributed to increasing government initiatives and supportive policies for gene therapy, growing availability of advanced gene delivery systems, increasing patient demand for effective and curative treatments, growing expansion of clinical trials targeting inherited disorders, and rising awareness among healthcare professionals about gene therapy benefits.

What Is The Gene Therapy For Inherited Genetic Disorders Market Growth Forecast?

The gene therapy for inherited genetic disorders market size is expected to see rapid growth in the next few years. It will grow to $8.15 billion in 2029 at a compound annual growth rate (CAGR) of 19.1%. The growth in the forecast period can be attributed to increasing prevalence of inherited genetic disorders, growing investment and funding in gene therapy research and development, increasing awareness and diagnosis rates of rare genetic diseases, rising approvals of novel gene therapy products by regulatory agencies, and growing adoption of personalized medicine approaches. Major trends in the forecast period include integration of advanced delivery systems for targeted gene therapy, developments in viral and non-viral vector technologies, advancements in next-generation sequencing enabling precise diagnosis, technology improvements in manufacturing and scalability of gene therapies, and integration of artificial intelligence to optimize gene therapy design.

Customer representative image Book your 30 minutes free consultation with our research experts

What’s The Trade War Impact On Pharmaceuticals Industry?

The sudden escalation of U.S. tariffs and the consequent trade frictions in spring 2025 are severely impacting the pharmaceutical companies contend with tariffs on APIs, glass vials, and lab equipment inputs with few alternative sources. Generic drug makers, operating on razor-thin margins, are especially vulnerable, with some reducing production of low-profit medicines. Biotech firms face delays in clinical trials due to tariff-related shortages of specialized reagents. In response, the industry is expanding API production in India and Europe, increasing inventory stockpiles, and pushing for trade exemptions for essential medicines.

How Is The Gene Therapy For Inherited Genetic Disorders Market Segmented?

1) By Type: Viral Vector-Based Therapies, Gene Editing Techniques, Ribonucleic Acid-Based Therapies, Ex Vivo Gene Therapy

2) By Application: Inherited Metabolic Disorders, Neurological Disorders, Cardiovascular Disorders, Musculoskeletal Disorders, Ophthalmic Disorders

3) By End-User: Hospitals, Specialty Clinics, Research Institutes, Other End-Users

Subsegments:

1) By Viral Vector-Based Therapies: Adenovirus Vectors, Adeno-Associated Virus (AAV) Vectors, Lentivirus Vectors

2) By Gene Editing Techniques: Zinc Finger Nucleases (ZFNs), Transcription Activator-Like Effector Nucleases (TALENs), Meganucleases

3) By Ribonucleic Acid-Based Therapies: Small Interfering Ribonucleic Acid, Antisense Oligonucleotides (ASOs), Messenger Ribonucleic Acid (mRNA) Therapies

4) By Ex Vivo Gene Therapy: Hematopoietic Stem Cell Gene Therapy, Mesenchymal Stem Cell Gene Therapy, Induced Pluripotent Stem Cell (iPSC) Therapy

What Is Driving The Gene Therapy For Inherited Genetic Disorders Market? Rising Demand For Personalized Medicine Driving Growth In The Market Due To Advancements In Genetic Technologies

The rising demand for personalized medicine is expected to propel the growth of the gene therapy for inherited genetic disorders market going forward. Personalized medicine refers to tailoring medical treatment to an individual’s genetic profile and personal characteristics for optimized care. Personalized medicine is increasing due to advancements in genetic technologies, making it easier and more affordable to tailor treatments to an individual’s unique genetic makeup. Personalized medicine boosts gene therapy by customizing treatments to each patient’s unique genetic profile, ensuring precise gene targeting and delivery while enhancing effectiveness and reducing side effects. For instance, in February 2024, according to the Personalized Medicine Coalition, a US-based non-profit organization, in 2023, the United States Food and Drug Administration (FDA) approved 16 new personalized treatments for rare disease patients, up from six in 2022. The newly approved personalized treatments for 2023 also include seven cancer drugs and three for other diseases and conditions. Therefore, the rising demand for personalized medicine is driving the growth of the gene therapy for inherited genetic disorders industry.

Who Are The Major Players In The Global Gene Therapy For Inherited Genetic Disorders Market?

Major companies operating in the gene therapy for inherited genetic disorders market are Sanofi S.A., Novartis AG, Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Genentech, Biomarin Pharmaceutical Inc, Sarepta Therapeutics Inc., Krystal Biotech Inc., Rocket Pharmaceuticals Inc., Sangamo Therapeutics Inc., REGENXBIO Inc., Passage Bio Inc., Voyager Therapeutics Inc., Generation Bio Co., Avrobio Inc, Editas Medicine Inc., MeiraGTx Holdings Plc, uniQure N.V., Intellia Therapeutics Inc., Bluebird Bio Inc, 4D Molecular Therapeutics Inc., CRISPR Therapeutics AG.

What Are The Key Trends Of The Global Gene Therapy For Inherited Genetic Disorders Market? Advancing Targeted Gene Therapies For Rare Inherited Genetic Disorders

Major companies operating in the gene therapy for inherited genetic disorders market are focusing on developing advanced solutions, such as gene therapy establishment, to create targeted, safer, and more effective treatments that address the root causes of genetic diseases. A gene therapy establishment refers to a biotechnology or pharmaceutical company that specializes in researching, developing, and commercializing gene therapy treatments aimed at correcting or modifying defective genes responsible for inherited genetic disorders. For instance, in November 2022, Replay, a US-based genome writing company, launched Telaria, a big DNA HSV gene therapy company. It is the second product company leveraging its high payload capacity herpes simplex virus (HSV) delivery vector, synHSV, and its lead indication is recessive dystrophic epidermolysis bullosa (RDEB), a severe genetic skin condition. The company was co-founded by leading HSV scientists and genetic skin disease experts, aiming to create transformative gene therapies for these rare skin diseases. This launch follows Replay's first gene therapy company, Eudora, which targets retinal diseases. The innovative structure of Replay separates technology development from therapeutic development within distinct product companies focused on specific disease areas.

Need data on a specific region in this market?

What Are Latest Mergers And Acquisitions In The Gene Therapy For Inherited Genetic Disorders Market? Ocuphire Pharma Inc. Acquired Opus Genetics Inc. To Accelerate Gene Therapy Development For Rare Retinal Diseases

In October 2024, Ocuphire Pharma Inc., a US-based biotechnology company, acquired Opus Genetics Inc. for an undisclosed amount. With this acquisition, Ocuphire Pharma aims to become a leader in developing and advancing gene therapies for rare inherited retinal diseases by combining Opus's innovative pipeline with its own development expertise. Opus Genetics Inc. is a US-based biotechnology company that offers gene therapy for inherited genetic disorders.

What Is The Regional Outlook For The Global Gene Therapy For Inherited Genetic Disorders Market?

North America was the largest region in the gene therapy for inherited genetic disorders market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in this market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa.

The countries covered in this market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

What Defines the Gene Therapy For Inherited Genetic Disorders Market?

The gene therapy for inherited genetic disorders market consists of revenues earned by entities by providing services such as genetic testing and diagnosis, personalized treatment planning, and gene delivery and administration. The market value includes the value of related goods sold by the service provider or included within the service offering. The gene therapy for inherited genetic disorders market also includes sales of zolgensma, luxturna, and strimvelis. Values in this market are ‘factory gate’ values, that is, the value of goods sold by the manufacturers or creators of the goods, whether to other entities (including downstream manufacturers, wholesalers, distributors, and retailers) or directly to end customers. The value of goods in this market includes related services sold by the creators of the goods.

How is Market Value Defined and Measured?

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

What is the Market Assessment and Strategic Outlook for the Gene Therapy For Inherited Genetic Disorders Industry?

The gene therapy for inherited genetic disorders market research report is one of a series of new reports from The Business Research Company that provides market statistics, including industry global market size, regional shares, competitors with the market share, detailed market segments, market trends and opportunities, and any further data you may need to thrive in the gene therapy for inherited genetic disorders industry. The market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future state of the industry.

Author : Abhilash Pyata

Gene Therapy For Inherited Genetic Disorders Market Report Forecast Analysis

Report AttributeDetails
Market Size Value In 2025 $4.05 billion
Revenue Forecast In 2034 $8.15 billion
Growth Rate CAGR of 19.1% from 2025 to 2034
Base Year For Estimation 2024
Actual Estimates/Historical Data 2019-2024
Forecast Period 2025 - 2029 - 2034
Market Representation Revenue in USD Billion and CAGR from 2025 to 2034
Segments Covered Type, Application, End-User
Regional Scope Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa
Country Scope The countries covered in the report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain. Additional countries that can be covered in the report are Bangladesh, Thailand, Vietnam, Malaysia, Singapore, Philippines, Hong Kong, New Zealand, Mexico, Chile, Argentina, Colombia, Peru, Austria, Belgium, Denmark, Finland, Ireland, Netherlands, Norway, Portugal, Sweden, Switzerland, Czech Republic, Poland, Romania, Ukraine, Saudi Arabia, Israel, Iran, Turkey, UAE, Egypt, Nigeria, South Africa.
Key Companies Profiled Sanofi S.A., Novartis AG, Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Genentech, Biomarin Pharmaceutical Inc, Sarepta Therapeutics Inc., Krystal Biotech Inc., Rocket Pharmaceuticals Inc., Sangamo Therapeutics Inc., REGENXBIO Inc., Passage Bio Inc., Voyager Therapeutics Inc., Generation Bio Co., Avrobio Inc, Editas Medicine Inc., MeiraGTx Holdings Plc, uniQure N.V., Intellia Therapeutics Inc., Bluebird Bio Inc, 4D Molecular Therapeutics Inc., CRISPR Therapeutics AG.
Customization ScopeRequest for Sample
Pricing And Purchase OptionsExplore Purchase Options

Table Of Contents

1. Executive Summary

2. Gene Therapy For Inherited Genetic Disorders Market Characteristics

3. Gene Therapy For Inherited Genetic Disorders Market Trends And Strategies

4. Gene Therapy For Inherited Genetic Disorders Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

4.1. Supply Chain Impact from Tariff War & Trade Protectionism

5. Global Gene Therapy For Inherited Genetic Disorders Growth Analysis And Strategic Analysis Framework

5.1. Global Gene Therapy For Inherited Genetic Disorders PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)

5.2. Analysis Of End Use Industries

5.3. Global Gene Therapy For Inherited Genetic Disorders Market Growth Rate Analysis

5.4. Global Gene Therapy For Inherited Genetic Disorders Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)

5.5. Global Gene Therapy For Inherited Genetic Disorders Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)

5.6. Global Gene Therapy For Inherited Genetic Disorders Total Addressable Market (TAM)

6. Gene Therapy For Inherited Genetic Disorders Market Segmentation

6.1. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Viral Vector-Based Therapies

Gene Editing Techniques

Ribonucleic Acid-Based Therapies

Ex Vivo Gene Therapy

6.2. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Inherited Metabolic Disorders

Neurological Disorders

Cardiovascular Disorders

Musculoskeletal Disorders

Ophthalmic Disorders

6.3. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Hospitals

Specialty Clinics

Research Institutes

Other End-Users

6.4. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Viral Vector-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Adenovirus Vectors

Adeno-Associated Virus (AAV) Vectors

Lentivirus Vectors

6.5. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Gene Editing Techniques, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Zinc Finger Nucleases (ZFNs)

Transcription Activator-Like Effector Nucleases (TALENs)

Meganucleases

6.6. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ribonucleic Acid-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Small Interfering Ribonucleic Acid

Antisense Oligonucleotides (ASOs)

Messenger Ribonucleic Acid (mRNA) Therapies

6.7. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ex Vivo Gene Therapy, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Hematopoietic Stem Cell Gene Therapy

Mesenchymal Stem Cell Gene Therapy

Induced Pluripotent Stem Cell (iPSC) Therapy

7. Gene Therapy For Inherited Genetic Disorders Market Regional And Country Analysis

7.1. Global Gene Therapy For Inherited Genetic Disorders Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

7.2. Global Gene Therapy For Inherited Genetic Disorders Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market

8.1. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market Overview

Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies

8.2. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8.3. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8.4. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

9. China Gene Therapy For Inherited Genetic Disorders Market

9.1. China Gene Therapy For Inherited Genetic Disorders Market Overview

9.2. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

9.3. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

9.4. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

10. India Gene Therapy For Inherited Genetic Disorders Market

10.1. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

10.2. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

10.3. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11. Japan Gene Therapy For Inherited Genetic Disorders Market

11.1. Japan Gene Therapy For Inherited Genetic Disorders Market Overview

11.2. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11.3. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11.4. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12. Australia Gene Therapy For Inherited Genetic Disorders Market

12.1. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12.2. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12.3. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13. Indonesia Gene Therapy For Inherited Genetic Disorders Market

13.1. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13.2. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13.3. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14. South Korea Gene Therapy For Inherited Genetic Disorders Market

14.1. South Korea Gene Therapy For Inherited Genetic Disorders Market Overview

14.2. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14.3. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14.4. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15. Western Europe Gene Therapy For Inherited Genetic Disorders Market

15.1. Western Europe Gene Therapy For Inherited Genetic Disorders Market Overview

15.2. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15.3. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15.4. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16. UK Gene Therapy For Inherited Genetic Disorders Market

16.1. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16.2. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16.3. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17. Germany Gene Therapy For Inherited Genetic Disorders Market

17.1. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17.2. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17.3. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18. France Gene Therapy For Inherited Genetic Disorders Market

18.1. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18.2. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18.3. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19. Italy Gene Therapy For Inherited Genetic Disorders Market

19.1. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19.2. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19.3. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20. Spain Gene Therapy For Inherited Genetic Disorders Market

20.1. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20.2. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20.3. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market

21.1. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market Overview

21.2. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21.3. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21.4. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22. Russia Gene Therapy For Inherited Genetic Disorders Market

22.1. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22.2. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22.3. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23. North America Gene Therapy For Inherited Genetic Disorders Market

23.1. North America Gene Therapy For Inherited Genetic Disorders Market Overview

23.2. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23.3. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23.4. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24. USA Gene Therapy For Inherited Genetic Disorders Market

24.1. USA Gene Therapy For Inherited Genetic Disorders Market Overview

24.2. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24.3. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24.4. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25. Canada Gene Therapy For Inherited Genetic Disorders Market

25.1. Canada Gene Therapy For Inherited Genetic Disorders Market Overview

25.2. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25.3. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25.4. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26. South America Gene Therapy For Inherited Genetic Disorders Market

26.1. South America Gene Therapy For Inherited Genetic Disorders Market Overview

26.2. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26.3. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26.4. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27. Brazil Gene Therapy For Inherited Genetic Disorders Market

27.1. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27.2. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27.3. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28. Middle East Gene Therapy For Inherited Genetic Disorders Market

28.1. Middle East Gene Therapy For Inherited Genetic Disorders Market Overview

28.2. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28.3. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28.4. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29. Africa Gene Therapy For Inherited Genetic Disorders Market

29.1. Africa Gene Therapy For Inherited Genetic Disorders Market Overview

29.2. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29.3. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29.4. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

30. Gene Therapy For Inherited Genetic Disorders Market Competitive Landscape And Company Profiles

30.1. Gene Therapy For Inherited Genetic Disorders Market Competitive Landscape

30.2. Gene Therapy For Inherited Genetic Disorders Market Company Profiles

30.2.1. Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis

30.2.2. Novartis AG Overview, Products and Services, Strategy and Financial Analysis

30.2.3. Astellas Pharma Inc. Overview, Products and Services, Strategy and Financial Analysis

30.2.4. Vertex Pharmaceuticals Incorporated Overview, Products and Services, Strategy and Financial Analysis

30.2.5. Genentech Overview, Products and Services, Strategy and Financial Analysis

31. Gene Therapy For Inherited Genetic Disorders Market Other Major And Innovative Companies

31.1. Biomarin Pharmaceutical Inc

31.2. Sarepta Therapeutics Inc.

31.3. Krystal Biotech Inc.

31.4. Rocket Pharmaceuticals Inc.

31.5. Sangamo Therapeutics Inc.

31.6. REGENXBIO Inc.

31.7. Passage Bio Inc.

31.8. Voyager Therapeutics Inc.

31.9. Generation Bio Co.

31.10. Avrobio Inc

31.11. Editas Medicine Inc.

31.12. MeiraGTx Holdings Plc

31.13. uniQure N.V.

31.14. Intellia Therapeutics Inc.

31.15. Bluebird Bio Inc

32. Global Gene Therapy For Inherited Genetic Disorders Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Gene Therapy For Inherited Genetic Disorders Market

34. Recent Developments In The Gene Therapy For Inherited Genetic Disorders Market

35. Gene Therapy For Inherited Genetic Disorders Market High Potential Countries, Segments and Strategies

35.1 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Countries Offering Most New Opportunities

35.2 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Segments Offering Most New Opportunities

35.3 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Growth Strategies

35.3.1 Market Trend Based Strategies

35.3.2 Competitor Strategies

36. Appendix

36.1. Abbreviations

36.2. Currencies

36.3. Historic And Forecast Inflation Rates

36.4. Research Inquiries

36.5. The Business Research Company

36.6. Copyright And Disclaimer

List Of Tables

    Table 1: Global Historic Market Growth, 2019-2024, $ Billion
  • Table 2: Global Forecast Market Growth, 2024-2029F, 2034F, $ Billion
  • Table 3: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 4: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 5: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 6: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Viral Vector-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 7: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Gene Editing Techniques, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 8: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ribonucleic Acid-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 9: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ex Vivo Gene Therapy, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 10: Global Gene Therapy For Inherited Genetic Disorders Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 11: Global Gene Therapy For Inherited Genetic Disorders Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 12: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 13: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 14: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 15: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 16: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 17: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 18: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 19: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 20: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 21: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 22: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 23: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 24: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 25: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 26: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 27: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 28: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 29: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 30: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 31: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 32: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 33: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 34: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 35: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 36: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 37: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 38: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 39: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 40: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 41: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 42: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 43: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 44: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 45: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 46: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 47: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 48: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 49: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 50: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 51: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 52: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 53: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 54: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 55: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 56: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 57: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 58: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 59: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 60: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 61: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 62: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 63: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 64: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 65: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 66: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 67: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 68: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 69: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 70: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 71: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 72: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 73: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 74: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 75: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 76: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 77: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Table 78: Sanofi S.A. Financial Performance
  • Table 79: Novartis AG Financial Performance
  • Table 80: Astellas Pharma Inc. Financial Performance
  • Table 81: Vertex Pharmaceuticals Incorporated Financial Performance
  • Table 82: Genentech Financial Performance

List Of Figures

    Figure 1: Global Historic Market Growth, 2019-2024, $ Billion
  • Figure 2: Global Forecast Market Growth, 2024-2029F, 2034F, $ Billion
  • Figure 3: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 4: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 5: Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 6: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Viral Vector-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 7: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Gene Editing Techniques, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 8: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ribonucleic Acid-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 9: Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ex Vivo Gene Therapy, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 10: Global Gene Therapy For Inherited Genetic Disorders Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 11: Global Gene Therapy For Inherited Genetic Disorders Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 12: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 13: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 14: Asia-Pacific, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 15: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 16: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 17: China, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 18: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 19: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 20: India, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 21: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 22: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 23: Japan, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 24: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 25: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 26: Australia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 27: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 28: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 29: Indonesia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 30: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 31: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 32: South Korea, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 33: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 34: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 35: Western Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 36: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 37: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 38: UK, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 39: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 40: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 41: Germany, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 42: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 43: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 44: France, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 45: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 46: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 47: Italy, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 48: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 49: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 50: Spain, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 51: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 52: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 53: Eastern Europe, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 54: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 55: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 56: Russia, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 57: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 58: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 59: North America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 60: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 61: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 62: USA, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 63: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 64: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 65: Canada, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 66: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 67: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 68: South America, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 69: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 70: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 71: Brazil, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 72: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 73: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 74: Middle East, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 75: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 76: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 77: Africa, Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
  • Figure 78: Sanofi S.A. Financial Performance
  • Figure 79: Novartis AG Financial Performance
  • Figure 80: Astellas Pharma Inc. Financial Performance
  • Figure 81: Vertex Pharmaceuticals Incorporated Financial Performance
  • Figure 82: Genentech Financial Performance

Frequently Asked Questions

Gene therapy for inherited genetic disorders is a medical strategy that targets the root cause of hereditary diseases by repairing or replacing faulty genes. Its main goal is to provide a potential cure rather than merely alleviating symptoms. It introduces functional genes into a patient’s cells, restores normal cell function, and improves overall health. This approach shows significant promise for treating rare genetic disorders, offering the possibility of long-lasting or permanent therapeutic effects. For further insights on this market, request a sample here

The market major growth driver - Rising Demand For Personalized Medicine Driving Growth In The Market Due To Advancements In Genetic Technologies. For further insights on this market, request a sample here

The gene therapy for inherited genetic disorders market size has grown rapidly in recent years. It will grow from $3.39 billion in 2024 to $4.05 billion in 2025 at a compound annual growth rate (CAGR) of 19.4%. The growth in the historic period can be attributed to increasing government initiatives and supportive policies for gene therapy, growing availability of advanced gene delivery systems, increasing patient demand for effective and curative treatments, growing expansion of clinical trials targeting inherited disorders, and rising awareness among healthcare professionals about gene therapy benefits. The gene therapy for inherited genetic disorders market size is expected to see rapid growth in the next few years. It will grow to $8.15 billion in 2029 at a compound annual growth rate (CAGR) of 19.1%. The growth in the forecast period can be attributed to increasing prevalence of inherited genetic disorders, growing investment and funding in gene therapy research and development, increasing awareness and diagnosis rates of rare genetic diseases, rising approvals of novel gene therapy products by regulatory agencies, and growing adoption of personalized medicine approaches. Major trends in the forecast period include integration of advanced delivery systems for targeted gene therapy, developments in viral and non-viral vector technologies, advancements in next-generation sequencing enabling precise diagnosis, technology improvements in manufacturing and scalability of gene therapies, and integration of artificial intelligence to optimize gene therapy design. For further insights on this market, request a sample here

The gene therapy for inherited genetic disorders market covered in this report is segmented
1) By Type: Viral Vector-Based Therapies, Gene Editing Techniques, Ribonucleic Acid-Based Therapies, Ex Vivo Gene Therapy
2) By Application: Inherited Metabolic Disorders, Neurological Disorders, Cardiovascular Disorders, Musculoskeletal Disorders, Ophthalmic Disorders
3) By End-User: Hospitals, Specialty Clinics, Research Institutes, Other End-Users Subsegments:
1) By Viral Vector-Based Therapies: Adenovirus Vectors, Adeno-Associated Virus (AAV) Vectors, Lentivirus Vectors
2) By Gene Editing Techniques: Zinc Finger Nucleases (ZFNs), Transcription Activator-Like Effector Nucleases (TALENs), Meganucleases
3) By Ribonucleic Acid-Based Therapies: Small Interfering Ribonucleic Acid, Antisense Oligonucleotides (ASOs), Messenger Ribonucleic Acid (mRNA) Therapies
4) By Ex Vivo Gene Therapy: Hematopoietic Stem Cell Gene Therapy, Mesenchymal Stem Cell Gene Therapy, Induced Pluripotent Stem Cell (iPSC) Therapy For further insights on this market,
request a sample here

North America was the largest region in the gene therapy for inherited genetic disorders market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in the gene therapy for inherited genetic disorders market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa. For further insights on this market, request a sample here.

Major companies operating in the gene therapy for inherited genetic disorders market are Sanofi S.A., Novartis AG, Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Genentech, Biomarin Pharmaceutical Inc, Sarepta Therapeutics Inc., Krystal Biotech Inc., Rocket Pharmaceuticals Inc., Sangamo Therapeutics Inc., REGENXBIO Inc., Passage Bio Inc., Voyager Therapeutics Inc., Generation Bio Co., Avrobio Inc, Editas Medicine Inc., MeiraGTx Holdings Plc, uniQure N.V., Intellia Therapeutics Inc., Bluebird Bio Inc, 4D Molecular Therapeutics Inc., CRISPR Therapeutics AG. . For further insights on this market, request a sample here.

Major trends in this market include Advancing Targeted Gene Therapies For Rare Inherited Genetic Disorders. For further insights on this market, request a sample here.

Customer representative image Book your 30 minutes free consultation with our research experts
Back to top WhatsApp icon