The GM1 Gangliosidosis Market Overview 2025 report reveals that the market size has grown significantly over the past few years, with projections indicating further expansion.
The size of the GM1 gangliosidosis market has experienced significant growth in recent years. The market increased from $0.51 billion in 2024 to $0.57 billion in 2025, with a compound annual growth rate (CAGR) of 11.4%.
The GM1 gangliosidosis market is predicted to reach $0.87 billion in 2029, with a compound annual growth rate (CAGR) of 11.1%.
Download Your Free Sample of the 2025 GM1 Gangliosidosis Market Report and Uncover Key Trends Now!The key drivers in the gm1 gangliosidosis market are:
• Increase in GM1 gangliosidosis cases and lysosomal storage disorders
• Rise in the number of clinical trials focused on this condition
• Emphasis on gene therapy and editing to combat the disease
• Increased adoption of genetic screening programs and advancements in personalized medicine
The GM1 gangliosidosis market covered in this report is segmented –
1) By Disease Type: Type 1 GM1 Gangliosidosis, Type 2 GMT Gangliosidosis, Type 3 GMT Gangliosidosis
2) By Treatment: Anticonvulsants, Bone Marrow Transplantation, Cord-Blood Hematopoietic Stem-Cell Transplantation, Enzyme Replacement, Gene Therapy
3) By End-User: Research Institutes, Hospitals, Other End-Users
Subsegments:
1) By Type 1 GM1 Gangliosidosis: Classic Infantile Onset, Atypical Infantile Onset
2) By Type 2 GM1 Gangliosidosis: Classic Juvenile Onset, Atypical Juvenile Onset
3) By Type 3 GM1 Gangliosidosis: Classic Adult Onset, Atypical Adult Onset
The key trends in the gm1 gangliosidosis market are:
• The future of the GM1 Gangliosidosis market is being shaped by advancements in gene-editing technologies.
• The integration of technology within the healthcare sector is an emerging trend.
• The market is witnessing advancement in diagnostic techniques.
• There is a noticeable trend towards developing advanced formulations and enhanced genetic therapies.
Major players in the gm1 gangliosidosis market are:
• Pfizer Inc.
• Sanofi S.A.
• Novartis AG
• Takeda Pharmaceutical Company Limited
• Sarepta Therapeutics Inc.
• CRISPR Therapeutics AG
• REGENXBIO Inc.
• Passage Bio Inc.
• Orchard Therapeutics plc
• AVROBIO Inc.
• uniQure N.V.
• GEMMA Biotherapeutics Inc.
• Lysogene S.A.
• AZAFAROS B.V.
• BioStrategies LC
• Sio Gene Therapies Inc.
• Gain Therapeutics Inc.
• Dorphan S.A.
• bluebird bio Inc.
• Axovant Gene Therapies Ltd.
• SphinCS GmbH.
North America was the largest region in the GM1 gangliosidosis market in 2024