Global Rare Disease Genome Editing Market Report 2025

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Rare Disease Genome Editing Global Market Report 2025

Name: Rare Disease Genome Editing Global Market Report 2025
Brand: The Business Research Company
Price: 4490.00 USD
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By Technology (Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, Transcription Activator-Like Effector Nucleases (TALEN), Zinc Finger Nucleases (ZFN), Other Technologies); By Disease Type (Monogenic Disorders, Multifactorial Disorders, Chromosomal Disorders); By Application (Therapeutics, Research); By End User ( Academic And Government Research Institutes); Subsegments:; By Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9); By Transcription Activator-Like Effector Nucleases (TALEN) (Standard Transcription Activator-Like Effector Nucleases (TALEN)); By Zinc Finger Nucleases (ZFN); By Other Technologies (Meganucleases) - Market Size, Trends, And Global Forecast 2025-2034

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report’s Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

Rare Disease Genome Editing Market Overview

• Rare Disease Genome Editing market size has reached to $1.09 billion in 2024

• Expected to grow to $2.46 billion in 2029 at a compound annual growth rate (CAGR) of 17.6%

• Growth Driver: Increasing Focus On Precision Medicine Fueling The Growth Of The Market Due To Advances In Genomic Sequencing And Biomarker Identification

• Market Trend: CRISPR-Based Gene Editing Enhances Precision And Outcomes

• North America was the largest region in 2024 and Asia-Pacific is the fastest growing region.

What Is Covered Under Rare Disease Genome Editing Market?

Rare disease genome editing refers to the use of precise genetic modification technologies to correct or alter disease-causing mutations in patients with rare genetic disorders. It helps to restore normal gene function, prevent disease progression, and develop personalized therapeutic solutions for conditions that currently have limited or no treatment options. This approach aims to address the root cause of the disease at the DNA level rather than managing symptoms.

The main technologies used in rare disease genome editing are clustered regularly interspaced short palindromic repeats (CRISPR) or CRISPR-associated protein 9, transcription activator-like effector nucleases (TALEN), zinc finger nucleases (ZFN), and others. Clustered regularly interspaced short palindromic repeats (CRISPR) or CRISPR-associated protein 9 is a genome editing tool that uses a guide RNA and the Cas9 enzyme to precisely cut and modify DNA for research and therapeutic purposes. It is used for different disease types such as monogenic disorders, multifactorial disorders, and chromosomal disorders, and finds application in therapeutics and research, serving end users such as biotechnology and pharmaceutical companies, academic and government research institutes, and hospitals.

Rare Disease Genome Editing Market Size and growth rate 2025 to 2029: Graph

What Is The Rare Disease Genome Editing Market Size 2025 And Growth Rate?

What Is The Rare Disease Genome Editing Market Growth Forecast?

The rare disease genome editing market size is expected to see rapid growth in the next few years. It will grow to $2.46 billion in 2029 at a compound annual growth rate (CAGR) of 17.6%. The growth in the forecast period can be attributed to increasing integration of AI in genome editing, rising demand for targeted therapies, growing advancements in gene delivery systems, increasing prevalence of multi-gene disorders, and rising focus on pediatric rare diseases. Major trends in the forecast period include advancements in multi-gene editing techniques, integration of AI-driven genomic analysis, technology-enabled personalized gene therapies, developments in in vivo gene delivery systems, and advancements in high-throughput genome screening.

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What’s The Trade War Impact On Pharmaceuticals Industry?

The sudden escalation of U.S. tariffs and the consequent trade frictions in spring 2025 are severely impacting the pharmaceutical companies contend with tariffs on APIs, glass vials, and lab equipment inputs with few alternative sources. Generic drug makers, operating on razor-thin margins, are especially vulnerable, with some reducing production of low-profit medicines. Biotech firms face delays in clinical trials due to tariff-related shortages of specialized reagents. In response, the industry is expanding API production in India and Europe, increasing inventory stockpiles, and pushing for trade exemptions for essential medicines.

How the Rare Disease Genome Editing Market Segmented?

1) By Technology: Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, Transcription Activator-Like Effector Nucleases (TALEN), Zinc Finger Nucleases (ZFN), Other Technologies

2) By Disease Type: Monogenic Disorders, Multifactorial Disorders, Chromosomal Disorders

3) By Application: Therapeutics, Research

4) By End User: Biotechnology And Pharmaceutical Companies, Academic And Government Research Institutes, Hospitals

Subsegments:

1) By Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9: Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 9, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 12, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 13, Base Editing, Prime Editing

2) By Transcription Activator-Like Effector Nucleases (TALEN): Standard Transcription Activator-Like Effector Nucleases (TALEN), Designer Transcription Activator-Like Effector Nucleases (dTALEN), Transcription Activator-Like Effector Nucleases (TALEN) Paired Nucleases

3) By Zinc Finger Nucleases (ZFN): Standard Zinc Finger Nucleases (ZFN), Engineered Zinc Finger Nucleases (ZFN), Modular Zinc Finger Nucleases (ZFN)

4) By Other Technologies: Meganucleases, Ribonucleic Acid (RNA)-Guided Nucleases, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Transposases

What Is Driving The Rare Disease Genome Editing Market? Increasing Focus On Precision Medicine Fueling The Growth Of The Market Due To Advances In Genomic Sequencing And Biomarker Identification

The increasing focus on precision medicine is expected to propel the growth of the rare disease genome editing market going forward. Precision medicine means tailoring prevention, diagnosis, and treatment to the individual’s genetic makeup, environment, and lifestyle. Precision medicine refers to a tailored healthcare approach that uses a patient’s genetics, environment, and lifestyle to provide more accurate and effective treatments. The increasing focus on precision medicine is due to advances in genomic sequencing and biomarker identification, as they enable precise detection and targeted therapies. Rare disease genome editing market supports precision medicine by enabling targeted correction of genetic mutations, making treatments more personalized and effective. It advances healthcare by addressing the root cause of rare disorders, improving patient outcomes and reducing reliance on symptomatic management. For instance, in March 2024, Novotech, an Australia-based biotechnology company, in 2023, 43% of the 217 FDA-approved oncology therapies were precision oncology treatments, with 78 incorporating DNA or NGS-detectable biomarkers. Therefore, the increasing focus on precision medicine is driving the growth of the rare disease genome editing industry.

Who Are The Major Players In The Global Rare Disease Genome Editing Market?

Major companies operating in the rare disease genome editing market are Regeneron Pharmaceuticals Inc., Sarepta Therapeutics Inc., Ultragenyx Pharmaceutical Inc., Beam Therapeutics Inc., CRISPR Therapeutics AG, Rocket Pharmaceuticals Inc., Sangamo Therapeutics Inc., Arcturus Therapeutics Holdings Inc., Editas Medicine Inc., Krystal Biotech Inc., Caribou Biosciences Inc, Bluebird Bio Inc., SpliceBio S.L., Cellectis SA, Generation Bio Co., iECURE Inc., Affinia Therapeutics Inc., Precision Biosciences Inc., Intellia Therapeutics Inc., and MeiraGTx Holdings plc.

What Are The Key Trends Of The Global Rare Disease Genome Editing Market? CRISPR-Based Gene Editing Enhances Precision And Outcomes

Major companies operating in the rare disease genome editing market are focusing on developing advanced therapeutic platforms, such as CRISPR-based gene editing systems, to enhance treatment precision, improve therapeutic outcomes, and address previously incurable genetic diseases. CRISPR-based gene editing systems refer to innovative technologies that enable precise modifications to the genome, allowing for the correction of genetic defects or the introduction of therapeutic genes into cells. For instance, in December 2023, Vertex Pharmaceuticals Inc., a US-based biopharmaceutical company, partnered with CRISPR Therapeutics Inc., a US-based biotechnology research company, and received conditional marketing authorization from the United Kingdom (U.K.) Medicines and Healthcare products Regulatory Agency (MHRA) for CASGEVY (exagamglogene autotemcel, exa-cel). It is indicated for patients aged 12 and older with sickle cell disease (SCD) and recurrent vaso-occlusive crises or transfusion-dependent beta thalassemia (TDT). Casgevy works by editing a patient’s hematopoietic stem cells to reactivate fetal hemoglobin production, which reduces or eliminates disease symptoms and offers a potential functional cure for these conditions.

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What Are Latest Mergers And Acquisitions In The Rare Disease Genome Editing Market? AstraZeneca Acquires Amolyt Pharma To Expand Rare Disease Pipeline In Endocrine Disorders

In November 2022, Alexion Pharmaceuticals Inc., a subsidiary of AstraZeneca plc, a US-based biopharmaceutical company, acquired LogicBio Therapeutics Inc. for an undisclosed sum. With this acquisition, Alexion Pharmaceuticals aims to expand in rare disease genomics and leverage LogicBio’s GeneRide platform for innovative therapies. LogicBio Therapeutics, Inc. is a US-based clinical-stage company specializing in developing genome-editing therapies for rare genetic disorders.

What Is The Regional Outlook For The Global Rare Disease Genome Editing Market?

North America was the largest region in the rare disease genome editing market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in this market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

What Defines the Rare Disease Genome Editing Market?

The rare disease genome editing market consists of revenues earned by entities by providing services such as gene editing therapy development, genetic testing and diagnostics, preclinical research and validation, clinical trial management, and regulatory consulting for genome-based therapeutics. The market value includes the value of related goods sold by the service provider or included within the service offering. The rare disease genome editing market also includes sales of zinc finger nucleases, delivery vectors, modified cells, and therapeutic genome-editing formulations. Values in this market are ‘factory gate’ values, that is the value of goods sold by the manufacturers or creators of the goods, whether to other entities (including downstream manufacturers, wholesalers, distributors and retailers) or directly to end customers. The value of goods in this market includes related services sold by the creators of the goods.

How is Market Value Defined and Measured?

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

What is the Market Assessment and Strategic Outlook for the Rare Disease Genome Editing Industry?

The rare disease genome editing market research report is one of a series of new reports from The Business Research Company that provides market statistics, including industry global market size, regional shares, competitors with the market share, detailed market segments, market trends and opportunities, and any further data you may need to thrive in the rare disease genome editing industry. The market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future state of the industry.

Author : Abhilash Pyata

1. Executive Summary

2. Rare Disease Genome Editing Market Characteristics

3. Rare Disease Genome Editing Market Trends And Strategies

4. Rare Disease Genome Editing Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

4.1. Supply Chain Impact from Tariff War & Trade Protectionism

5. Global Rare Disease Genome Editing Growth Analysis And Strategic Analysis Framework

5.1. Global Rare Disease Genome Editing PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)

5.2. Analysis Of End Use Industries

5.3. Global Rare Disease Genome Editing Market Growth Rate Analysis

5.4. Global Rare Disease Genome Editing Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)

5.5. Global Rare Disease Genome Editing Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)

5.6. Global Rare Disease Genome Editing Total Addressable Market (TAM)

6. Rare Disease Genome Editing Market Segmentation

6.1. Global Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9

Transcription Activator-Like Effector Nucleases (TALEN)

Zinc Finger Nucleases (ZFN)

Other Technologies

6.2. Global Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Monogenic Disorders

Multifactorial Disorders

Chromosomal Disorders

6.3. Global Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Therapeutics

Research

6.4. Global Rare Disease Genome Editing Market, Segmentation By End User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Biotechnology And Pharmaceutical Companies

Academic And Government Research Institutes

Hospitals

6.5. Global Rare Disease Genome Editing Market, Sub-Segmentation Of Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 9

Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 12

Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 13

Base Editing

Prime Editing

6.6. Global Rare Disease Genome Editing Market, Sub-Segmentation Of Transcription Activator-Like Effector Nucleases (TALEN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Standard Transcription Activator-Like Effector Nucleases (TALEN)

Designer Transcription Activator-Like Effector Nucleases (dTALEN)

Transcription Activator-Like Effector Nucleases (TALEN) Paired Nucleases

6.7. Global Rare Disease Genome Editing Market, Sub-Segmentation Of Zinc Finger Nucleases (ZFN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Standard Zinc Finger Nucleases (ZFN)

Engineered Zinc Finger Nucleases (ZFN)

Modular Zinc Finger Nucleases (ZFN)

6.8. Global Rare Disease Genome Editing Market, Sub-Segmentation Of Other Technologies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Meganucleases

Ribonucleic Acid (RNA)-Guided Nucleases

Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Transposases

7. Rare Disease Genome Editing Market Regional And Country Analysis

7.1. Global Rare Disease Genome Editing Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

7.2. Global Rare Disease Genome Editing Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8. Asia-Pacific Rare Disease Genome Editing Market

8.1. Asia-Pacific Rare Disease Genome Editing Market Overview

Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies

8.2. Asia-Pacific Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8.3. Asia-Pacific Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8.4. Asia-Pacific Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

9. China Rare Disease Genome Editing Market

9.1. China Rare Disease Genome Editing Market Overview

9.2. China Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

9.3. China Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

9.4. China Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

10. India Rare Disease Genome Editing Market

10.1. India Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

10.2. India Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

10.3. India Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11. Japan Rare Disease Genome Editing Market

11.1. Japan Rare Disease Genome Editing Market Overview

11.2. Japan Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11.3. Japan Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11.4. Japan Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12. Australia Rare Disease Genome Editing Market

12.1. Australia Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12.2. Australia Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12.3. Australia Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13. Indonesia Rare Disease Genome Editing Market

13.1. Indonesia Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13.2. Indonesia Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13.3. Indonesia Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14. South Korea Rare Disease Genome Editing Market

14.1. South Korea Rare Disease Genome Editing Market Overview

14.2. South Korea Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14.3. South Korea Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14.4. South Korea Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15. Western Europe Rare Disease Genome Editing Market

15.1. Western Europe Rare Disease Genome Editing Market Overview

15.2. Western Europe Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15.3. Western Europe Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15.4. Western Europe Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16. UK Rare Disease Genome Editing Market

16.1. UK Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16.2. UK Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16.3. UK Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17. Germany Rare Disease Genome Editing Market

17.1. Germany Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17.2. Germany Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17.3. Germany Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18. France Rare Disease Genome Editing Market

18.1. France Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18.2. France Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18.3. France Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19. Italy Rare Disease Genome Editing Market

19.1. Italy Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19.2. Italy Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19.3. Italy Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20. Spain Rare Disease Genome Editing Market

20.1. Spain Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20.2. Spain Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20.3. Spain Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21. Eastern Europe Rare Disease Genome Editing Market

21.1. Eastern Europe Rare Disease Genome Editing Market Overview

21.2. Eastern Europe Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21.3. Eastern Europe Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21.4. Eastern Europe Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22. Russia Rare Disease Genome Editing Market

22.1. Russia Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22.2. Russia Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22.3. Russia Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23. North America Rare Disease Genome Editing Market

23.1. North America Rare Disease Genome Editing Market Overview

23.2. North America Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23.3. North America Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23.4. North America Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24. USA Rare Disease Genome Editing Market

24.1. USA Rare Disease Genome Editing Market Overview

24.2. USA Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24.3. USA Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24.4. USA Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25. Canada Rare Disease Genome Editing Market

25.1. Canada Rare Disease Genome Editing Market Overview

25.2. Canada Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25.3. Canada Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25.4. Canada Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26. South America Rare Disease Genome Editing Market

26.1. South America Rare Disease Genome Editing Market Overview

26.2. South America Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26.3. South America Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26.4. South America Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27. Brazil Rare Disease Genome Editing Market

27.1. Brazil Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27.2. Brazil Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27.3. Brazil Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28. Middle East Rare Disease Genome Editing Market

28.1. Middle East Rare Disease Genome Editing Market Overview

28.2. Middle East Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28.3. Middle East Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28.4. Middle East Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29. Africa Rare Disease Genome Editing Market

29.1. Africa Rare Disease Genome Editing Market Overview

29.2. Africa Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29.3. Africa Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29.4. Africa Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

30. Rare Disease Genome Editing Market Competitive Landscape And Company Profiles

30.1. Rare Disease Genome Editing Market Competitive Landscape

30.2. Rare Disease Genome Editing Market Company Profiles

30.2.1. Regeneron Pharmaceuticals Inc. Overview, Products and Services, Strategy and Financial Analysis

30.2.2. Sarepta Therapeutics Inc. Overview, Products and Services, Strategy and Financial Analysis

30.2.3. Ultragenyx Pharmaceutical Inc. Overview, Products and Services, Strategy and Financial Analysis

30.2.4. Beam Therapeutics Inc. Overview, Products and Services, Strategy and Financial Analysis

30.2.5. CRISPR Therapeutics AG Overview, Products and Services, Strategy and Financial Analysis

31. Rare Disease Genome Editing Market Other Major And Innovative Companies

31.1. Rocket Pharmaceuticals Inc.

31.2. Sangamo Therapeutics Inc.

31.3. Arcturus Therapeutics Holdings Inc.

31.4. Editas Medicine Inc.

31.5. Krystal Biotech Inc.

31.6. Caribou Biosciences Inc

31.7. Bluebird Bio Inc.

31.8. SpliceBio S.L.

31.9. Cellectis SA

31.10. Generation Bio Co.

31.11. iECURE Inc.

31.12. Affinia Therapeutics Inc.

31.13. Precision Biosciences Inc.

31.14. Intellia Therapeutics Inc.

31.15. MeiraGTx Holdings plc

32. Global Rare Disease Genome Editing Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Rare Disease Genome Editing Market

34. Recent Developments In The Rare Disease Genome Editing Market

35. Rare Disease Genome Editing Market High Potential Countries, Segments and Strategies

35.1 Rare Disease Genome Editing Market In 2029 - Countries Offering Most New Opportunities

35.2 Rare Disease Genome Editing Market In 2029 - Segments Offering Most New Opportunities

35.3 Rare Disease Genome Editing Market In 2029 - Growth Strategies

35.3.1 Market Trend Based Strategies

35.3.2 Competitor Strategies

36. Appendix

36.1. Abbreviations

36.2. Currencies

36.3. Historic And Forecast Inflation Rates

36.4. Research Inquiries

36.5. The Business Research Company

36.6. Copyright And Disclaimer

List Of Tables

Table 1: Global Historic Market Growth, 2019-2024, $ Billion

Table 2: Global Forecast Market Growth, 2024-2029F, 2034F, $ Billion

Table 3: Global Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 4: Global Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 5: Global Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 6: Global Rare Disease Genome Editing Market, Segmentation By End User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 7: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 8: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Transcription Activator-Like Effector Nucleases (TALEN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 9: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Zinc Finger Nucleases (ZFN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 10: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Other Technologies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 11: Global Rare Disease Genome Editing Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 12: Global Rare Disease Genome Editing Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 13: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 14: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 15: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 16: China, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 17: China, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 18: China, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 19: India, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 20: India, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 21: India, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 22: Japan, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 23: Japan, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 24: Japan, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 25: Australia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 26: Australia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 27: Australia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 28: Indonesia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 29: Indonesia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 30: Indonesia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 31: South Korea, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 32: South Korea, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 33: South Korea, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 34: Western Europe, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 35: Western Europe, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 36: Western Europe, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 37: UK, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 38: UK, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 39: UK, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 40: Germany, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 41: Germany, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 42: Germany, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 43: France, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 44: France, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 45: France, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 46: Italy, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 47: Italy, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 48: Italy, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 49: Spain, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 50: Spain, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 51: Spain, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 52: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 53: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 54: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 55: Russia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 56: Russia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 57: Russia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 58: North America, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 59: North America, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 60: North America, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 61: USA, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 62: USA, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 63: USA, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 64: Canada, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 65: Canada, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 66: Canada, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 67: South America, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 68: South America, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 69: South America, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 70: Brazil, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 71: Brazil, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 72: Brazil, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 73: Middle East, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 74: Middle East, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 75: Middle East, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 76: Africa, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 77: Africa, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 78: Africa, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Table 79: Regeneron Pharmaceuticals Inc. Financial Performance

Table 80: Sarepta Therapeutics Inc. Financial Performance

Table 81: Ultragenyx Pharmaceutical Inc. Financial Performance

Table 82: Beam Therapeutics Inc. Financial Performance

Table 83: CRISPR Therapeutics AG Financial Performance

List Of Figures

Figure 1: Global Historic Market Growth, 2019-2024, $ Billion

Figure 2: Global Forecast Market Growth, 2024-2029F, 2034F, $ Billion

Figure 3: Global Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 4: Global Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 5: Global Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 6: Global Rare Disease Genome Editing Market, Segmentation By End User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 7: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 8: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Transcription Activator-Like Effector Nucleases (TALEN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 9: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Zinc Finger Nucleases (ZFN), By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 10: Global Rare Disease Genome Editing Market, Sub-Segmentation Of Other Technologies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 11: Global Rare Disease Genome Editing Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 12: Global Rare Disease Genome Editing Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 13: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 14: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 15: Asia-Pacific, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 16: China, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 17: China, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 18: China, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 19: India, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 20: India, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 21: India, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 22: Japan, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 23: Japan, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 24: Japan, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 25: Australia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 26: Australia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 27: Australia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 28: Indonesia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 29: Indonesia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 30: Indonesia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 31: South Korea, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 32: South Korea, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 33: South Korea, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 34: Western Europe, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 35: Western Europe, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 36: Western Europe, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 37: UK, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 38: UK, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 39: UK, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 40: Germany, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 41: Germany, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 42: Germany, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 43: France, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 44: France, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 45: France, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 46: Italy, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 47: Italy, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 48: Italy, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 49: Spain, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 50: Spain, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 51: Spain, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 52: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 53: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 54: Eastern Europe, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 55: Russia, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 56: Russia, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 57: Russia, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 58: North America, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 59: North America, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 60: North America, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 61: USA, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 62: USA, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 63: USA, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 64: Canada, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 65: Canada, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 66: Canada, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 67: South America, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 68: South America, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 69: South America, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 70: Brazil, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 71: Brazil, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 72: Brazil, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 73: Middle East, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 74: Middle East, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 75: Middle East, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 76: Africa, Rare Disease Genome Editing Market, Segmentation By Technology, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 77: Africa, Rare Disease Genome Editing Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 78: Africa, Rare Disease Genome Editing Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

Figure 79: Regeneron Pharmaceuticals Inc. Financial Performance

Figure 80: Sarepta Therapeutics Inc. Financial Performance

Figure 81: Ultragenyx Pharmaceutical Inc. Financial Performance

Figure 82: Beam Therapeutics Inc. Financial Performance

Figure 83: CRISPR Therapeutics AG Financial Performance

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Frequently Asked Questions

What is the definition of the Rare Disease Genome Editing market?

How will the Rare Disease Genome Editing market drivers and restraints affect the market dynamics? What forces will shape the Rare Disease Genome Editing industry going forward?

The market major growth driver - Increasing Focus On Precision Medicine Fueling The Growth Of The Market Due To Advances In Genomic Sequencing And Biomarker Identification. For further insights on this market, request a sample here

What is the forecast market size or the forecast market value of the Rare Disease Genome Editing market?

The rare disease genome editing market size has grown rapidly in recent years. It will grow from $1.09 billion in 2024 to $1.29 billion in 2025 at a compound annual growth rate (CAGR) of 17.9%. The growth in the historic period can be attributed to increasing government funding for genetic research, rising awareness of rare disease diagnosis, increasing collaboration between biotech companies, and rising investment in personalized medicine. The rare disease genome editing market size is expected to see rapid growth in the next few years. It will grow to $2.46 billion in 2029 at a compound annual growth rate (CAGR) of 17.6%. The growth in the forecast period can be attributed to increasing integration of AI in genome editing, rising demand for targeted therapies, growing advancements in gene delivery systems, increasing prevalence of multi-gene disorders, and rising focus on pediatric rare diseases. Major trends in the forecast period include advancements in multi-gene editing techniques, integration of AI-driven genomic analysis, technology-enabled personalized gene therapies, developments in in vivo gene delivery systems, and advancements in high-throughput genome screening. For further insights on this market, request a sample here

How is the Rare Disease Genome Editing market segmented?

The rare disease genome editing market covered in this report is segmented as
1) By Technology: Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9, Transcription Activator-Like Effector Nucleases (TALEN), Zinc Finger Nucleases (ZFN), Other Technologies
2) By Disease Type: Monogenic Disorders, Multifactorial Disorders, Chromosomal Disorders
3) By Application: Therapeutics, Research
4) By End User: Biotechnology And Pharmaceutical Companies, Academic And Government Research Institutes, Hospitals Subsegments:
1) By Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) Or CRISPR-Associated Protein 9: Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 9, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 12, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Protein 13, Base Editing, Prime Editing
2) By Transcription Activator-Like Effector Nucleases (TALEN): Standard Transcription Activator-Like Effector Nucleases (TALEN), Designer Transcription Activator-Like Effector Nucleases (dTALEN), Transcription Activator-Like Effector Nucleases (TALEN) Paired Nucleases
3) By Zinc Finger Nucleases (ZFN): Standard Zinc Finger Nucleases (ZFN), Engineered Zinc Finger Nucleases (ZFN), Modular Zinc Finger Nucleases (ZFN)
4) By Other Technologies: Meganucleases, Ribonucleic Acid (RNA)-Guided Nucleases, Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)-Associated Transposases For further insights on this market, request a sample here

Which region has the largest share of the Rare Disease Genome Editing market? What are the other regions covered in the report?

North America was the largest region in the rare disease genome editing market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in rare disease genome editing report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa. For further insights on this market, request a sample here.

Who are the major players in the Rare Disease Genome Editing market?

What are the key trends in the Rare Disease Genome Editing market?

Major trends in this market include CRISPR-Based Gene Editing Enhances Precision And Outcomes For further insights on this market, request a sample here.